EMERGING PUBLIC BIOTECH

REGENXBIO INC (RGNX)

Rockville, United States · North America
RARE DISEASE
EMERGING PUBLIC BIOTECH
HEADQUARTERS
Rockville, United States
TICKER
RGNX
SEGMENT
Emerging Public Biotech
THERAPY AREAS
Rare Disease
COMPANY OVERVIEW

REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapies that deliver functional genes to cells with genetic defects in the United States. Its gene therapy product candidates are based on NAV Technology Platform, a proprietary adeno-associated virus gene delivery platform. The company's products in pipeline includes ABBV-RGX-314 for the treatment of wet age-related macular degeneration, diabetic retinopathy, and other chronic retinal diseases; and RGX-202 for the treatment of Duchenne muscular dystrophy, as well as RGX-121 for the treatment of mucopolysaccharidosis type II. It also develops RGX-111 for the treatment of mucopolysaccharidosis type I. In addition, the company licenses its NAV Technology Platform to other biotechnology and pharmaceutical companies. Furth…

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