EMERGING PUBLIC BIOTECH

ROCKET PHARMACEUTICALS INC (RCKT)

Cranbury, United States · North America
RARE DISEASE
EMERGING PUBLIC BIOTECH
HEADQUARTERS
Cranbury, United States
TICKER
RCKT
SEGMENT
Emerging Public Biotech
THERAPY AREAS
Rare Disease
COMPANY OVERVIEW

Rocket Pharmaceuticals, Inc., together with its subsidiaries, operates as a late-stage biotechnology company that focuses on developing, manufacturing, and selling of genetic therapies for rare and devastating diseases in the United States. It develops in vivo adeno-associated viral (AAV) programs, which include programs for Danon disease (DD), a multi-organ lysosomal-associated disorder leading to early death due to heart failure (RP-A501), which is in Phase 2 trial; Plakophilin-2 Arrhythmogenic Cardiomyopathy (PKP2-ACM), an inheritable cardiac disorder that is characterized by a progressive loss of cardiac muscle mass, severe right ventricular dilation, dysplasia, fibrofatty replacement of the myocardium and a high propensity to arrhythmias and sudden death (RP-A601), which is in phase 1…

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