ACTIVE SUBSTANCE / INN

ETUVETIDIGENE AUTOTEMCEL

Brand name(s): Waskyra
EMA LISTED
AUTHORISED
Wiskott-Aldrich Syndrome
ACTIVE SUBSTANCE
Etuvetidigene Autotemcel
REGULATORS
EMA
SPONSORS / MAH
Fondazione Telethon ETS
TOTAL APPLICATIONS
1
EMA AUTHORISATIONS
PRODUCT NAMEHOLDERSTATUSDATEINDICATION
WaskyraFondazione Telethon ETSAuthorised09/01/2026Wiskott-Aldrich Syndrome

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