ACTIVE SUBSTANCE / INN

EXAGAMGLOGENE AUTOTEMCEL

Brand name(s): Casgevy
EMA LISTED
AUTHORISED
beta-Thalassemia;Anemia, Sickle Cell
ACTIVE SUBSTANCE
Exagamglogene Autotemcel
REGULATORS
EMA
SPONSORS / MAH
Vertex Pharmaceuticals (Ireland) Limited
TOTAL APPLICATIONS
1
EMA AUTHORISATIONS
PRODUCT NAMEHOLDERSTATUSDATEINDICATION
CasgevyVertex Pharmaceuticals (Ireland) LimitedAuthorised09/02/2024beta-Thalassemia;Anemia, Sickle Cell

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