ACTIVE SUBSTANCE / INN

L-ACETYLLEUCINE

Brand name(s): Aqneursa
EMA LISTED
AUTHORISED
Niemann-Pick Disease, Type C
ACTIVE SUBSTANCE
L-Acetylleucine
REGULATORS
EMA
SPONSORS / MAH
Intrabio Ireland Limited
TOTAL APPLICATIONS
1
EMA AUTHORISATIONS
PRODUCT NAMEHOLDERSTATUSDATEINDICATION
AqneursaIntrabio Ireland LimitedAuthorised19/01/2026Niemann-Pick Disease, Type C

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