Sarepta Therapeutics
Biotech focused on Duchenne muscular dystrophy and other rare neuromuscular diseases.
Therapeutic areas
Selected products and programs
Linked curated drug profiles
Selected active clinical trials
Phase 3 · Active Not Recruiting · Limb-girdle Muscular Dystrophy
Study of SRP-1003 in Participants With Type 1 Myotonic DystrophyPhase 1 · Recruiting · Myotonic Dystrophy 1
A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's DiseasePhase 1 · Recruiting · Huntington's Disease
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory CohortPhase 1 · Recruiting · Duchenne Muscular Dystrophy
Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular Dystrophy Type 1Phase 1 · Recruiting · Muscular Dystrophy, Facioscapulohumeral
A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)Phase 3 · Active Not Recruiting · Muscular Dystrophy, Duchenne
Selected patent records
golodirsen · Expires 2028-06-28
US RE48468eteplirsen · Expires 2028-10-27
US RE47769eteplirsen · Expires 2029-02-02
US 10337003eteplirsen · Expires 2034-03-14
US 10364431eteplirsen · Expires 2034-03-14
US 9506058eteplirsen · Expires 2034-03-14
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